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Making an Impact for the Rare Disease Community

Developing breakthrough therapies for rare diseases is only possible because of the tireless efforts of our global community of researchers and scientists, advocates and caregivers, and most importantly our patients.

Now, as part of AstraZeneca, we have the potential to impact the lives of even more people around the world.

Our Philosophy   

Every day, we're inspired to think differently and follow the science to transform the lives of people around the world living with a rare disease. These three tenets continue to guide our decisions.

Patients First

Our patients and caregivers are at the center of all we do. They're the experts in the rare diseases journey, and our decisions are guided by what we hear is important to them.

Science + Innovation

We follow the science through the discovery, development and delivery of life-changing medicines, and continue to push boundaries across disease areas with significant unmet needs.

Health Equity

We aim to improve equity and health outcomes for people living with rare diseases by focusing on reducing the time to diagnosis, improving access to care, and engaging stakeholders globally to amplify impact.

our-legacy

Our Legacy

Our pioneering legacy in rare diseases is rooted in being the first to translate the complex biology of the complement system into transformative medicines.

Today, we continue to push the boundaries of science, building a diversified pipeline across disease areas with significant unmet need, using an array of innovative modalities.

Our Vision

We believe it takes radical collaboration among all in the rare disease community to create more life-changing therapies, a more equitable healthcare system, and broader global awareness. It's why we work so closely with patients, advocacy groups, and world-renowned research teams to ensure the greatest possible impact.

Our People

We are innovators, leaders and collaborators helping to change the world for people living with rare diseases.

Veeva ID: GL/ALL/0051