Inspired Every Day

The work we do is guided by people living with rare and devastating diseases. We are driven to continuously innovate and create meaningful value in all we do to help patients and families fully live their best lives.

SEE THEIR STORIES
  • Tanner, diagnosed with HPP at 4 days old, with a stuffed animal

    My hope for Tanner in the future is that he enters into adulthood. I kind of hope that he will be a doctor and maybe help kids like doctors have helped him.”

    RENE, MOM OF TANNER

    LIVING WITH HPP

    TANNER
    LIVING WITH HPP

  • Roberta, diagnosed with gMG at 16 years old

    This experience has taught me to look at the small things that count. Now, I feel that I have something to look forward to and I am who I want to be.”

    ROBERTA

    LIVING WITH gMG

    ROBERTA
    LIVING WITH GMG

  • The Trendys, diagnosed at 17, 14, 11, and 9 with LAL-D

    Now we knew what we were up against, we knew we could fight.”

    REBECCA, MOM OF TRENDY BROTHERS

    LIVING WITH LAL-D

    THE TRENDY FAMILY
    LIVING WITH LAL-D

  • Chelsey, living with NMOSD, painting

    I don't define myself as having a rare disease. It’s part of my life, but it’s certainly not who I am.”

    CHELSEY

    LIVING WITH NMOSD

    CHELSEY
    LIVING WITH NMOSD

  • Donnan, diagnosed with aHUS at 39 years old, and his son

    I can chase my kids and play again. I think knowing what I have brings a peace to my life.”

    DONNAN

    LIVING WITH aHUS

    DONNAN
    LIVING WITH aHUS

Every day, those who live with rare diseases and devastating conditions inspire us to push the boundaries of medicine, technology, and healthcare services. Our goal is to transform their reality for the better.

5

APPROVED MEDICINES

7

RARE DISEASES & DEVASTATING CONDITIONS

25+

OFFICES WORLDWIDE

3000+

TALENTED COLLEAGUES

Everyday Stories

Two women at a computer

Our legacy in rare disease is rooted in being the first to translate the complex biology of the complement system into transformative medicines. The complement system is a part of the immune system and is essential to the body’s defense against infection.

Learn More
 
MORE NEWS
Jesse, diagnosed with gMG
I feel like tomorrow I can do something, whereas before, I didn’t feel like tomorrow was possible.”
JESSE LIVING WITH gMG