#RallyforRare

The simplest gesture.
A world of difference.

Every day we’re inspired by all of those affected by rare and devastating diseases. On this Rare Disease Day, we raise our hands and #RallyforRare to show our collective support.

Pursuing Groundbreaking Innovation

Through the transformative power of our science, we have delivered life-changing therapies to patients suffering from rare diseases—diseases that often affect families for generations. We have pioneered the complex field of complement biology and delivered solutions to challenges that once seemed impossible for patients with devastating complement-mediated and metabolic disorders.

Creating a Lasting Impact

The dedication and passion of our employees enable us to achieve our mission. We are building a rewarding place to work where people are empowered to make a difference and where diversity of backgrounds and ideas is encouraged.

Serving Patients Today and the Generations That Follow

Patients with rare diseases are our guiding star. They inspire us every day to find answers, and we act with integrity, urgency, and discipline because we know their lives are at stake.