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Our Inspiration
- Living With Rare Diseases
- Real Stories
  - NF1
  - aHUS
  - gMG
  - HPP
  - LAL-D
  - NMOSD
  - PNH
- Support Services
Albie, one of our guiding stars

When Albie was born, his mom, Charlotte, said that he was “absolutely fine. Everything was fine for about two weeks.”
Our Medicines
- Conditions We Treat
  - aHUS
  - gMG
  - HPP
  - LAL-D
  - NF1 PN
  - NMOSD
  - PNH
- Medicines
Our medicines help people like Donnan

As a father of two young children, Donnan recalls being afraid of what the future would hold prior to his diagnosis.
Our Research
We innovate for Ruthie

Married with a newborn son, Ruthie was scared to learn that PNH was a life-threatening illness that at the time had no approved treatment.
Our Commitment
We give back for families like Evie's

At only three months old, Evie's parents were told that her case was severe and that there were no approved or effective treatment options.
Our Company
Roberta is our inspiration

Despite having a constant struggle with symptoms, Roberta revisited her dreams and put herself through nursing school.
Your Career
- Career Opportunities
  - Join Our Team
- Working Here
  - Benefits
  - Culture
Make a difference for families like Tristan's

Tristan's parents experienced a whirlwind of emotions and fear after learning their 5-year-old son had such a rare and serious disease.

LEADERSHIP

Guiding Us to a Better Future, Every Day

Management Team

Our management team is a talented, diverse, and experienced group of leaders who bring vast expertise across every aspect of our business and operations and a commitment to advance our mission of serving people living with rare diseases and their families.

Marc Dunoyer

Chief Executive Officer

Soraya Bekkali

SVP, International Commercial Operations

Seng H. Cheng

SVP, Head of Research and Product Development

Fred Chereau

SVP, Strategy & Business Development

Sean Christie

Chief Financial and Administration Officer

Ruth-Diazaraque

Ruth Diazaraque

VP, Research and Development

Shane Doyle

SVP, Head of Operations

Nicola Heffron

SVP, Head of Global Marketing & Market Access

Christophe Hotermans

SVP, Medical Affairs

Kimihiro Kasamo

VP & General Manager, Japan

Simone Lauchart

VP, Project & Portfolio Management

Sarah Marshall

VP, Head of Human Resources

Gianluca Pirozzi

Gianluca Pirozzi

SVP, Head of Development, Regulatory and Safety

Todd Spalding

SVP, Deputy General Counsel

Tamar Thompson

VP, Head of Corporate Affairs

Scott Weintraub

SVP, US Commercial Operations

I’m hoping my story will inspire others to continue to fight for themselves.”

KIM LIVING WITH NMOSD

HEAR HER STORY