To transform the lives of people affected by rare diseases and devastating conditions by continuously innovating and creating meaningful value in all that we do.
Our research and development is fueled by a relentless sense of urgency and an steadfast commitment to helping more rare disease patients and their families around the world.
Learn how we are addressing some of today’s most pressing rare disease challenges by investigating in new targets, modalities and technologies, with more opportunities for innovation than ever before.
Patient Support • June 25, 2024
Getting to know Chathuri Daluwatte, an Alexion R&D Leading Voice
Patient Support • February 05, 2025
Addressing the Unmet Needs of the Amyloidosis Community
Patient Support • September 23, 2024
Shortening the Path to Diagnosis in Rare Disease
Research and Development • September 18, 2024
Getting to know Nick France, an Alexion R&D Leading Voice
Research and Development • June 08, 2024
Getting to know Seng Cheng, an Alexion R&D Leading Voice
Patient Support • April 18, 2024
The voices and perspectives of patients play an essential role in rare disease research and development (R&D).
Patient Support • April 16, 2024
Diagnostics and artificial intelligence (AI) systems are transforming research and development (R&D) in the healthcare industry.
Health Equity • February 06, 2024
Collectively, more than 400 million people around the world are living with a rare disease, defined as conditions that affect a small number of people compared to the general population.
Patient Support • November 08, 2023
Science is hard, but rare disease research and development (R&D) stands apart. Because individual patient populations are small and many rare diseases are not well understood, research in this space can often bring added complexity.
Clinical Trials • November 07, 2023
Why is conducting clinical trials for rare diseases difficult? Because studying a rare disease poses unique challenges and requires thinking differently.
Clinical Trials • November 01, 2023
Alexion’s leadership in rare disease is driven by the many individuals whose expertise, creativity and tenacity fuel our commitment to advancing innovative science.
Veeva ID: GL/ALL/0071